SKC sponsors the congress "Orphan Drugs & Rare Diseases Global 2019 Europe"

0.05% - this is the number that defines whether a disease is rare. In the European Union, a disease is classified as rare if it affects no more than 5 out of 10,000 people. Often there is no prospect of cure and existing treatment options are limited. For this reason, simplified HTA procedures exist in Germany and the EU for bringing orphan drugs onto the market.

Due to the heterogeneity of the diseases, the difficulty in collecting study data and the spatial distribution of experts, events such as the "Orphan Drugs & Rare Diseases Global Congress 2019 Europe" are of particular importance. It provides the perfect opportunity for the various stakeholders to come together and improve treatment options for rare diseases. For this reason, SKC consulting supports this year's congress as a Gold Sponsor.

Workshops, discussions and lectures on the core topics "macro outlook and trends", "policy framework and collaboration", "clinical development for orphan drugs", "market access, pricing and reimbursement" will take place in London from the 4th to the 6th of March 2019.

Prof. Dr. Matthias P. Schönermark, chairperson of the event and managing partner of SKC consulting, will hold a presentation and highlight possible solutions for the reimbursement of orphans, gene therapies and drugs for advanced therapies. He will also be discussing "Pricing and Return on Investment (ROI) of Orphan Drugs: What is the right pricing strategy for orphan drug manufacturers to treat patients while remaining economically viable" in a panel discussion.

SKC consulting looks forward to fresh input and stimulating conversations. Further information on Orphan Drugs in Germany can be found in our White Paper: "Orphan Drugs in Germany - lessons learned from AMNOG, best and worst practices and strategic implications".

BY Prof. Matthias P. Schönermark, M.D., Ph.D., managing director and Dipl.-Kauffrau Karolin Priese

Sources:
Orphan Drugs & Rare Diseases Global Congress 2019 Europe
Bundesgesundheitsministerium: Seltene Erkrankungen
Die deutschen Universitätsklinika: Seltene Erkrankungen